What we do:
- Animal models of muscular diseases and gene therapy approaches
- Induced pluripotent stem cell-based in vitro models of neuromuscular and muscular diseases (Disease in a Dish).
- Diseases under study include Duchene muscular dystrophy, limb-girdle muscular dystrophy, distal arthrogryposis, ALS, Alzheimer’s disease and Charcot-Marie-Tooth disease.
